An organization focused on a fatal genetic disorder that affects men has launched a mobile app that allows for the location of clinical trials and clinics.
British drug maker Shire is working with Cambridge, Mass.-based Acceleron Pharma to develop treatments for...
A mid-stage clinical trial of a drug for muscular dystrophy got mixed results, developers Genzyme...
GlaxoSmithKline has identified more than 5,500 rare diseases it could potentially target as part of...