Content about Familial amyloid polyneuropathy

June 19, 2012

FDA declines to approve Pfizer's tafamidis meglumine

The Food and Drug Administration has declined to approve a drug designed to treat a rare, progressive and fatal neurodegenerative disease.

May 29, 2012

FDA panel backs Pfizer drug for rare genetic disease

An experimental drug made by Pfizer for a rare and fatal neurodegenerative disease got a favorable vote from a Food and Drug Administration expert panel.

February 15, 2012

FDA accepts Pfizer application for genetic disease drug

The Food and Drug Administration will review a regulatory approval application from Pfizer for a drug to treat an extremely rare and fatal degenerative disease, Pfizer said Wednesday.